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NAGLU
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Clinical and genetic features of 13 patients with mucopolysaccarhidosis type IIIB: Description of tw…
Murine cellular model of mucopolysaccharidosis, type IIIB (MPS IIIB) - A preliminary study with part…
Iminosugar C-Glycosides Work as Pharmacological Chaperones of NAGLU, a Glycosidase Involved in MPS I…
Downregulation of NAGLU in VEC Increases Abnormal Accumulation of Lysosomes and Represents a Predict…
Cell-Mediated Immunity to NAGLU Transgene Following Intracerebral Gene Therapy in Children With Muco…
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Intracerebral Gene Therapy in Children With Sanfilippo Type B Syndrome
Gene Transfer Clinical Trial for Mucopolysaccharidosis (MPS) IIIB
A Retrospective Chart Review of Deceased Patients With Mucopolysaccharidosis Type IIIB
Natural History Studies of Mucopolysaccharidosis III
Evaluation of Blood Brain Barrier Integrity and Structural Abnormalities in MPS IIIB Patients Using …
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