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QuickView for SMN2 (gene)
Most Relevant Literature
- Reproductive findings in male animals exposed to selective survival of motor neuron 2 (SMN2) gene sp…
- PRMT inhibitor promotes SMN2 exon 7 inclusion and synergizes with nusinersen to rescue SMA mice.
- Discovery of a CNS penetrant small molecule SMN2 splicing modulator with improved tolerability for s…
- A phase 1 healthy male volunteer single escalating dose study of the pharmacokinetics and pharmacody…
- Base editing rescue of spinal muscular atrophy in cells and in mice.
Most Relevant Clinical Trials
- Pre-Symptomatic Study of Intravenous Onasemnogene Abeparvovec-xioi in Spinal Muscular Atrophy (SMA) …
- Single-Dose Gene Replacement Therapy Using for Patients With Spinal Muscular Atrophy Type 1 With One…
- Quantitative Analysis of SMN1 and SMN2 Gene Based on DHPLC System
- Effect of Low-Dose Celecoxib on SMN2 in Patients With Spinal Muscular Atrophy
- Study to Evaluate Sodium Phenylbutyrate in Pre-symptomatic Infants With Spinal Muscular Atrophy
