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deficiency of N- acetylgalactosamine- 6- sulfatase
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There were no matches for deficiency of N- acetylgalactosamine- 6- sulfatase
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Evidence of epigenetic landscape shifts in mucopolysaccharidosis IIIB and IVA.
Mucopolysaccharidosis IVA: Current Disease Models and Drawbacks.
Efficient CRISPR/Cas9 nickase-mediated genome editing in an in vitro model of mucopolysaccharidosis …
Consensus statement on enzyme replacement therapy for mucopolysaccharidosis IVA in Central and South…
Enhanced Efficiency of the Basal and Induced Apoptosis Process in Mucopolysaccharidosis IVA and IVB …
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Study of Recombinant Human N-acetylgalactosamine 4-sulfatase (rhASB) in Patients With MPS VI
Natural History of Atypical Morquio A Disease
Non-invasive Functional Assessment and Pathogenesis of Morquio A
Study of rhASB in Patients With Mucopolysaccharidosis VI
BMN 110 Phase 3B in Australian Patients
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