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gene therapy
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Curated Studies
Most Correlated Studies
Mucosal associated invariant T cells of patients after HCT with and without acute GVHD
Chromosome 5q deletion in therapy-related myeloid neoplasms (t-MN)
Peripheral blood CD34+ cells from Polycythemia Vera patients
Bone marrow cells from therapy-related acute myeloid leukemia cases with trisomy 8
Murine SCCVII cells in pre- and non-irradiated stroma
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Literature
Most Relevant Literature
Gene-targeted therapies: Towards equitable development, diagnosis, and access.
Advances in designing Adeno-associated viral vectors for development of anti-HBV gene therapeutics.
Magnetic field-assisted gene delivery: achievements and therapeutic potential.
Gene therapies for mucopolysaccharidoses.
Restoring Ciliary Function: Gene Therapeutics for Primary Ciliary Dyskinesia.
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Clinical Trials
Most Relevant Clinical Trials
Lentiviral Gene Therapy for Epilepsy
AAV Gene Therapy Screening/Observational Protocol (ECLIPSE)
Gene Therapy for Haemophilia A.
Gene Therapy for Chronic Granulomatous Disease
Gene Therapy for Tay-Sachs Disease
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