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mucopolysaccharidosis iiib
NextBio Summary
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Six regions of the brain from mucopolysaccharidosis type VII GUSB-mutant mice
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Proteomic Analysis of Mucopolysaccharidosis IIIB Mouse Brain.
Temporospatial Development of Neuropathologic Findings in a Canine Model of Mucopolysaccharidosis II…
An exonic insertion in the NAGLU gene causing Mucopolysaccharidosis IIIB in Schipperke dogs.
Macrophage enzyme and reduced inflammation drive brain correction of mucopolysaccharidosis IIIB by s…
Heparan Sulfate, Mucopolysaccharidosis IIIB and Sulfur Metabolism Disorders.
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A Study of Mucopolysaccharidosis Type IIIB (MPS IIIB)
A Treatment Extension Study of Mucopolysaccharidosis Type IIIB
A Treatment Study of Mucopolysaccharidosis Type IIIB
A Prospective Natural History Study of Mucopolysaccharidosis Type IIIB (MPS IIIB)
Safety, Pharmacokinetics, and Pharmacodynamics/Efficacy of SBC-103 in Mucopolysaccharidosis III, Typ…
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