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Dystroglycan
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Deletion of POMT2 in Zebrafish Causes Degeneration of Photoreceptors.
A novel 1-bp deletion variant in DAG1 in Japanese familial asymptomatic hyper-CK-emia.
Sarcospan increases laminin-binding capacity of α-dystroglycan to ameliorate DMD independent of Galg…
Tyrosine phosphorylation as a regulator of dystrophin and beta-dystroglycan interaction: A molecular…
The lymph node stromal laminin α5 shapes alloimmunity.
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Clinical Trial Readiness for the Dystroglycanopathies
Congenital Muscle Disease Study of Patient and Family Reported Medical Information
Intravenous Immune Globulin to Treat Hereditary Inclusion Body Myopathy
Open Label Phase 2 Study of BBP-418 in Patients With LGMD2I
Biomarker Development in LGMD2i
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