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PFIC- 2
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Curated Studies
Most Correlated Studies
Liver explant tissue from adult and pediatric choelstatic liver disease
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Literature
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Bsep/Abcb11 knockout ameliorates Schistosoma mansoni liver pathology by reducing parasite fecundity.
Cav-1 regulates the bile salt export pump on the canalicular membrane of hepatocytes by PKCĪ±-associa…
An Enhancer Within Abcb11 Regulates G6pc2 in C57BL/6 Mouse Pancreatic Islets.
miR-199a-5p inhibits the expression of ABCB11 in obstructive cholestasis.
Pharmacological Premature Termination Codon Readthrough of ABCB11 in Bile Salt Export Pump Deficienc…
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This Study Will Investigate the Efficacy and Safety of A4250 in Children With PFIC 1 or 2
A Study of TAK-625 for the Treatment of Progressive Familial Intrahepatic Cholestasis (PFIC)
Long Term Safety & Efficacy Study Evaluating The Effect of A4250 in Children With PFIC
A Placebo-controlled Study of Maralixibat (SHP625) in Pediatric Subjects With Progressive Familial I…
Progressive Familial Intrahepatic Cholestasis in Indian Children - Establishing an Indian PFIC Regis…
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