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Sarcoglycans
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Genetic Markers
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Curated Studies
Most Correlated Studies
Cardiac and arota mesoangioblasts from beta sarcoglycan null and wildtype mice
Mesoangioblasts derived from iPSCs of patients with limb-girdle muscular dystrophy 2D (LGMD2D)
Histone deacetylase 4 represses dystrophin-glycoprotein (DGC) complex expression
Aorta from atherosclerotic APOE null mice
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Literature
Most Relevant Literature
Immunofluorescence signal intensity measurements as a semi-quantitative tool to assess sarcoglycan c…
Novel γ-sarcoglycan interactors in murine muscle membranes.
The sarcoglycan complex in skeletal muscle.
Muscle Diversity, Heterogeneity, and Gradients: Learning from Sarcoglycanopathies.
The multiple twists in the tale: Brain iron accumulation, facial jerks, and truncal dystonia.
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Clinical Trials
Most Relevant Clinical Trials
Clinical Study of AAV1-gamma-sarcoglycan Gene Therapy for Limb Girdle Muscular Dystrophy Type 2C
Gene Delivery Clinical Trial of SRP-9003 (Bidridistrogene Xeboparvovec) for Participants With Limb-G…
A Gene Transfer Single Dose Study to Evaluate the Safety, Tolerability and Efficacy of SRP-9003 in N…
Gene Transfer Therapy for Treating Children and Adults With Limb Girdle Muscular Dystrophy Type 2D (…
A Gene Transfer Therapy Study to Evaluate the Safety of SRP-9004 (Patidistrogene Bexoparvovec) in Pa…
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