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diamond- blackfan anemia
Summary
General Info
Curated Studies
Most Correlated Studies
OMIM - Anemia disorders
OMIM - Congenital disorder
OMIM - Anemias
Dermal fibroblasts from Diamond-Blackfan anemia patients
Lymphoblastoid cells from blood of diamond blackfan anemia disease subjects
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Literature
Most Relevant Literature
Diamond-Blackfan Anemia: 2 Cases With a Twist.
Diamond-Blackfan anemia, the archetype of ribosomopathy: How distinct is it from the other constitut…
Understanding complex disease-related mechanisms: Rational therapies for Diamond-Blackfan anaemia.
Animal models of Diamond-Blackfan anemia: updates and challenges.
Normal Erythroid Precursors in Diamond-Blackfan Anemia: A Rare Case Highlighting Challenges That Rem…
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Clinical Trials
Most Relevant Clinical Trials
L-leucine in Diamond Blackfan Anemia Patients
Diamond Blackfan Anemia Registry (DBAR)
Treatment of Refractory Diamond-Blackfan Anemia With Eltrombopag
Rituximab to Treat Moderate Aplastic Anemia, Pure Red Cell Aplasia, or Diamond Blackfan Anemia
Study of the Selective GlyT1 Inhibitor Bitopertin for Steroid-Refractory Diamond-Blackfan Anemia
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