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GM1
Summary
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Curated Studies
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Mouse Phenotypes - GM1 gangliosidosis
OMIM - Congenital disorder
OMIM - Metabolic disease
Monocytes treated with microvesicles isolated from differentiated macrophages.
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Literature
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Sialidase NEU3 action on GM1 ganglioside is neuroprotective in GM1 gangliosidosis.
Natural history of GM1 gangliosidosis-Retrospective cohort study of 61 French patients from 1998 to …
Turning the spotlight on the oligosaccharide chain of GM1 ganglioside.
Chemical control over Asialo-GM1: A dual ligand for pili and Lectin A that activates swarming motili…
The natural history of Type 1 infantile GM1 gangliosidosis: A literature-based meta-analysis.
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Clinical Trials
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GM1 Prophylaxis for WBRT Related Cognitive Dysfunction
Natural History Study of Infantile and Juvenile GM1 Gangliosidosis (GM1) Patients
GM1 Ganglioside Effects on Parkinson's Disease
Study of Safety, Tolerability and Efficacy of PBGM01 in Pediatric Subjects With GM1 Gangliosidosis
Interviews and Video Capture in Patients With GM1 Gangliosidosis
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